SAPROPTERIN | SAPROPTERIN | NATURAL MOLECULE (link) ATC A16AX07
METABOLISM AGONIST TREATMENT OF HYPERPHENYLALANINAEMIA (HPA) REDUCTION OF PHENYLALANINE CONCENTRATION IN PATIENTS WITH PHENYLKETONURIA (PKU) COFACTOR FOR THE ENZYME PHENYLALANINE HYDROXYLASE (PAH). TREATMENT WITH BH4 CAN ACTIVATE RESIDUAL PAH AND IMPROVE THE NORMAL OXIDATIVE METABOLISM OF PHE, AND DECREASE PHE LEVELS TREATMENT OF TETRAHYDROBIOPTERIN (BH4) DEFICIENCY | ORAL | Tmax 3.5 HOUR HT 6.7 HOUR SOLUBILITY SOLUBLE IN WATER | PHENYLALANINE HYDROXYLASE | PHENYLALANINE-4-HYDROXYLASE ACTIVATOR CHEMBL3076 PHENYLALANINE-4-HYDROXYLASE P00439 PHENYLALANINE-4-HYDROXYLASE HOMO SAPIENS ENZYME REDUCTASE | EMA ANSM (in French) Inxight Drugs Dailymed Drugs.com SIDER side effects Chemical Probes Portal ChEMBL BindingDB DrugBank |